Ladders to Cures Accelerator Symposium: Keynote - Jonathan Weissman @broadinstitute

Uploaded June 2025 | Updated September 2026, 2 weeks ago

Ladders to Cures Accelerator Symposium: Reaching New Heights
Friday, May 16, 2025
Broad Institute

Introduction by Anna Greka, Broad Institute

Keynote 1: Brainwide Silencing of Prion Protein by AAV-Mediated Delivery of an Engineered Compact Epigenetic Editor

Jonathan Weissman
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We are excited to invite you to the second annual Ladder to Cures Symposium | Reaching New Heights whose goal is to share progress in scalable technologies and advances in biology leading to treatments and cures for patients with rare genetic diseases. This hybrid all-day event will be held on May 16th, 2025 in the Broad Auditorium and streamed online. Anyone with an interest in rare disease research is invited to attend.

Building on Broad’s strengths of scaling scientific efforts to accelerate progress, this symposium will convene scientists, physicians, patients/patient-led foundations and advisors from the biopharma and regulatory space to join the conversation.

For more information visit: broadinstitute.org/L2C

Copyright Broad Institute, 2025. All rights reserved.

Ladders to Cures Accelerator Symposium: Keynote - Jonathan Weissman

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