Uploaded January 2026 | Updated September 2026, 2 weeks ago
A family from Slovenia traveled to Nemours Children’s Hospital, Florida to pursue FDA-approved Elevidys gene therapy for Duchenne muscular dystrophy (DMD). Through our International Medicine Program, we help families from around the world access advanced pediatric treatments not available in their home countries.
Duchenne muscular dystrophy is a rare genetic disorder that causes progressive muscle weakness. Gene therapy offers new hope by targeting the underlying genetic cause of the disease.
Our International Medicine Program supports families at every step, from medical coordination and travel planning to interpreter services and personalized care, ensuring children receive world-class treatment in a compassionate environment.
To learn more about our International Medicine Program, visit: nemours.org/international-hospitals-for-children.html
At Nemours Children's, we’re redefining children's health by looking beyond and improving children’s health where it starts — at home, in the community and anywhere you find children. To discover more about Nemours and how we're making a difference, visit: nemours.org
A family from Slovenia traveled to Nemours Children’s Hospital, Florida to pursue FDA-approved Elevidys gene therapy for Duchenne muscular dystrophy (DMD). Through our International Medicine Program, we help families from around the world access advanced pediatric treatments not available in their home countries.
Duchenne muscular dystrophy is a rare genetic disorder that causes progressive muscle weakness. Gene therapy offers new hope by targeting the underlying genetic cause of the disease.
Our International Medicine Program supports families at every step, from medical coordination and travel planning to interpreter services and personalized care, ensuring children receive world-class treatment in a compassionate environment.
To learn more about our International Medicine Program, visit: nemours.org/international-hospitals-for-children.html
At Nemours Children's, we’re redefining children's health by looking beyond and improving children’s health where it starts — at home, in the community and anywhere you find children. To discover more about Nemours and how we're making a difference, visit: nemours.org
