Uploaded December 2016 | Updated September 2026, 2 weeks ago
yourekascience.org/portfolio/cut-and-paste-treating-spinal-muscular-atrophy
In order to make protein, the gibberish portions of RNA are removed to create a coherent message. This is called RNA splicing. RNA splicing of a specific gene is defective in Spinal Muscular Atrophy. Find out how a new drug called "nusinersen" is attempting to repair this splicing defect.
This video was produced in collaboration with Cold Spring Harbor Laboratory.
yourekascience.org/portfolio/cut-and-paste-treating-spinal-muscular-atrophy
In order to make protein, the gibberish portions of RNA are removed to create a coherent message. This is called RNA splicing. RNA splicing of a specific gene is defective in Spinal Muscular Atrophy. Find out how a new drug called "nusinersen" is attempting to repair this splicing defect.
This video was produced in collaboration with Cold Spring Harbor Laboratory.
