Uploaded June 2024 | Updated September 2026, 1 day ago

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From the 2024 International Bone Marrow Failure Scientific Symposium: ADVANCES IN PAROXYSMAL NOCTURNAL HEMOGLOBINURIA

Featured speakers:
Morag Griffin, MBChB, FRCPath - St James’s University Hospital, UK
How to choose among C5 inhibitors

Regis Peffault de Latour, MD, PhD - Hôpital Saint Louis, FRANCE
Proximal inhibitors: add-on or monotherapy? Front-line or second line?

Camilla Frieri, MD - AORN S. Giuseppe Moscati Avellino, ITALY
Is there a role for transplant in PNH?

Ronald Taylor, PhD - UNIVERSITY OF VIRGINIA
Identifying therapeutic targets in the complement cascade

Pedro Prata, MD - Hôpital Saint Louis, FRANCE
Germline complement gene variants in PNH